FDA Approves World’s First Crispr Gene-Editing Drug for Sickle-Cell Disease
www.wsj.com
The U.S. has approved the world’s first medicine employing Crispr technology, a Nobel Prize-winning discovery that promised a powerful new tool to treat disease.

The key thing about this kind of therapy is that it’s not a drug you keep on taking - it’s a one-time thing which permanently cures the disease.

  • Dem Bosain@midwest.socialEnglish
    5·
    11 months ago

    It’s very expensive, but it’s also a very intensive treatment. As I understand, they harvest stem cells, and those are modified with CRISPR. Meanwhile, they give the patient chemo-therapy to destroy all the bone-marrow. Then the modified stem-cells are placed in the body to regenerate the bone marrow.

    I’m not educated to understand any of this, so hopefully someone can expand.